Globin gene transfer as a potential treatment for the β-thalassaemias and sickle cell disease.
M Sadelain - Vox sanguinis, 2004 - search.ebscohost.com
M Sadelain
Vox sanguinis, 2004•search.ebscohost.comThe article discusses the transfer of globin gene as treatment potential for the β-
thalassaemias and sickle cell diseases, in the United States. The β-thalassaemias and
sickle cell diseases are congenital anaemias that resulted from the deficiency or altered
synthesis of the haemoglobin β chain. In serious haemoglobinopathy, studies from
laboratories certify to the efficacy in the transfer of globin gene in mouse models.
thalassaemias and sickle cell diseases, in the United States. The β-thalassaemias and
sickle cell diseases are congenital anaemias that resulted from the deficiency or altered
synthesis of the haemoglobin β chain. In serious haemoglobinopathy, studies from
laboratories certify to the efficacy in the transfer of globin gene in mouse models.
Abstract
The article discusses the transfer of globin gene as treatment potential for the β-thalassaemias and sickle cell diseases, in the United States. The β-thalassaemias and sickle cell diseases are congenital anaemias that resulted from the deficiency or altered synthesis of the haemoglobin β chain. In serious haemoglobinopathy, studies from laboratories certify to the efficacy in the transfer of globin gene in mouse models.
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